WORLDSymposium is designed for basic, translational and clinical researchers, patient advocacy groups, clinicians, and all others who are interested in learning more about the latest discoveries related to lysosomal diseases and the clinical investigation of these advances. Each year, WORLDSymposium presents the latest information from basic science, translational research, and clinical trials for lysosomal diseases.

Development and preliminary analysis from the Batten disease CLN1 registry. Scott Snyder, Emily de los Reyes and Sean Ekins

Pre-clinical development of an enzyme replacement therapy for CLN1 Batten disease: Process development, stability and uptake studies Renuka Raman, Ben Horst, Maryam Zare, Zahra Shahrokh, Magdalena Leszcyniecka and Sean Ekins

In poster session 

Wednesday, 5 February, 2025 from 15:30-17:30 Pacific Standard Time(PST)